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Question:

First clinical gene therapy was given in 1992 to a 4 years old girl for Adenine deficiency, Adenosine deficiency, Adenosine deaminase deficiency, or Growth deficiency?

Growth deficiency

Adenosine deaminase deficiency

Adenosine deficiency

Adenine deficiency

Solution:

Gene therapy is a procedure of introducing copies of a healthy gene to replace defective gene responsible for disease development. The first clinical gene transfer took place on 22nd May 1992 for correction of adenosine deaminase (ADA) enzyme deficiency.